Substrate reduction therapy involves the reduction or elimination of substances that are usually broken down by enzymes. In diseases where there is a deficiency of enzymes and where Enzyme Replacement Therapy has failed, SRT is used to reduce the accumulation of such substances that would normally be broken down (digested) within the body prior to toxic levels developing. An example of SRT is the drug Zavesca (Miglustat) that is used in the treatment of Gaucher disease.
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